One Shot, Lifetime Relief: How Zynteglo Ended a 12-Year-Old’s Pain

Researchers at the Children’s Hospital of Philadelphia have unveiled Zynteglo, an FDA-approved gene therapy that “cures” beta-thalassemia by reprogramming a patient’s own stem cells to produce healthy hemoglobin. In a one-time treatment, clinicians harvest bone-marrow stem cells, insert a correct copy of the beta-globin gene in the lab, then reinfuse the cells after a brief […]