One Shot, Lifetime Relief: How Zynteglo Ended a 12-Year-Old’s Pain

Researchers at the Children’s Hospital of Philadelphia have unveiled Zynteglo, an FDA-approved gene therapy that “cures” beta-thalassemia by reprogramming a patient’s own stem cells to produce healthy hemoglobin. Beta-thalassemia is a genetic blood disorder where the body cannot produce enough beta-globin, a key part of hemoglobin — the protein in red blood cells that carries […]